Disease Focus Areas

Targeting serious conditions stemming from protein misfolding, where our therapeutic approach can make a meaningful difference.

Disease Focus Areas

We target a range of serious conditions stemming from protein misfolding, where our therapeutic approach can make a meaningful difference.

AL Amyloidosis

Our lead program targeting light chain amyloidosis with PROT-001.

Myopathy & Cardiomyopathy

Addressing muscle and heart conditions caused by protein dysfunction.

Stroke & Renal Disease

Targeting protein misfolding in cerebrovascular and kidney disorders.

Retinal Conditions

Developing treatments for vision-threatening protein misfolding diseases.

Channelopathies

Restoring proper function of ion channel proteins.

Degenerative Diseases

Combating progressive conditions linked to protein aggregation.